Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Β-Thalassemias | NEJM
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
Introductory Chapter: β-Thalassemia | IntechOpen
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
